In the U.S., a condition is considered a rare disease if it affects fewer than 200,000 people nationwide at any given time.  The Office of Rare Diseases Research at the National Institutes of Health reports that there are approximately 7,000 rare diseases known today, and sometimes a diagnosis of a rare disease can take months or even years. Among them are approximately ten million children who are affected by a rare disease. Many rare children’s disease does not have a known treatment at this time for several reasons. Most of the clinical research studies do not address the specific pediatric populations, and children’s rare disease patients are few and located in various geographic areas. Key in your information to educate yourself facts online games casino. Additionally, many rare diseases do not have a clear underlying cause.  This makes research in this year more critical.

The definition of children’s rare disease is that (A) the disease is a serious or life-threatening disease in which the serious or life-threatening manifestations primarily affect individuals aged from birth to 18 years, including age groups often called neonates, infants, children, and adolescents {and} (B) The disease is a rare disease or condition per US law definition.

Some examples of children’s rare disease are:

•Batten Disease

•Biliary Atresia

•CANDLE Syndrome
•Childhood Interstitial Lung Disease
•Duchenne muscular dystrophy
•Krabbe Disease

Please follow the following link to search for all the children’s rare diseases.

Browse A-Z | Genetic and Rare Diseases Information Center (GARD) – an NCATS Program (