Rare Disease Institute in Children’s National Hospital now is seeing patients at their their new location on the Research & Innovation Campus, 7125 13th Pl NW Washington, DC 20012.
Rare Disease Institute - Genetics and Metabolism | Children's National Hospital
National Organization for Rare Disorders (NORD) will host Rare Disease Breakthrough Summit on Oct 18-19 this year.
You can search any pediatric rare disease designation at FDA database
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Search Orphan Drug Designations and Approvals (fda.gov)
FDA Approves First Treatment for Rare Genetic Metabolic Pediatric Disorder (ajmc.com)
